Preclinical Study Suggests Stem Cell Therapy EN001 and Insulin May Improve Symptoms of Charcot-Marie-Tooth Disease Type 1A
Eplontersen Exceeds Established Thresholds for Symptom and Disability Improvement in ATTRv-PN
ATTRv-PN Treatment Vutrisiran Demonstrates Long-Term Efficacy in Open-Label HELIOS-A Extension
Defining Remyelination in the Context of Multiple Sclerosis