Neuromuscular

The NeurologyLive neuromuscular disease clinical focus page offers updates and information related to the clinical care and management of individuals with neuromuscular diseases such as amyotrophic lateral sclerosis, Duchenne muscular dystrophy, cerebral palsy, and spinal muscular atrophy, as well as rare diseases. This page consists of news, podcasts, and videos about the latest FDA actions, clinical guideline updates, interviews with physicians, study and clinical trial findings, and more.

Episode 37: The Impact of Awareness Efforts in ALS

"Mind Moments," a podcast from NeurologyLive, brings you an exclusive interview with Matthew B. Harms, MD.

Case-Based Insights: Expert Perspectives on the Treatment of Adult-Onset SMA

Expert neurologists discuss patient cases involving the treatment of adult-onset spinal muscular atrophy (SMA).

NeuroVoices: Yung Chyung, MD, on the Advantages of Apitegromab in Early SMA Treatment

The chief medical officer of Scholar Rock described how the investigational apitegromab aims to fill some of the current unmet needs for patients with spinal muscular atrophy.

NeurologyLive® Friday 5 — November 26, 2021

November 26, 2021

Article

Take 5 minutes to catch up on NeurologyLive®'s highlights from the week ending November 26, 2021.

This Week on NeurologyLive® — November 22, 2021

November 22, 2021

Article

Here's what is coming soon to NeurologyLive®.

NeurologyLive® Friday 5 — November 19, 2021

November 19, 2021

Article

Take 5 minutes to catch up on NeurologyLive®'s highlights from the week ending November 19, 2021.

This Week on NeurologyLive — November 15, 2021

November 15, 2021

Article

Here's what is coming soon to NeurologyLive.

PXT3003 Meets Phase 3 Primary End Point in Charcot-Marie-Tooth Disease Type 1A

November 14, 2021

Article

Despite being discontinued early, patients in the high-dose group of the PLEO-CMT trial experienced statistically significant improvement in Overall Neuropathy Limitations Scale total score.

RBD Shows No Impact Post-DBS, Erenumab Superior to Topiramate, ADORE Phase 3 Trial Begins

November 13, 2021

Video

Neurology News Network for the week ending November 13, 2021.

Robert Califf, MD, Nominated by Biden Administration as Next FDA Commissioner

November 12, 2021

Article

Having previously served as head of the organization during the Obama administration, Califf will replace current Acting Commissioner Janet Woodcock, MD.

NeurologyLive Friday 5 — November 12, 2021

November 12, 2021

Article

Take 5 minutes to catch up on NeurologyLive's highlights from the week ending November 12, 2021.

A New Treatment in ALS: AMX0035’s Pending FDA Decision

November 11, 2021

Article

After Amylyx submitted an NDA for the combination therapy, Justin Klee and Josh Cohen, the cofounders and co-chief operating officers of the company, shared their perspectives.

Phase 3 ADORE Trial of FNP122 in ALS Enrolls First Patient

November 10, 2021

Article

The trial is anticipated to enroll 300 patients with amyotrophic lateral sclerosis in Europe to evaluate the safety and efficacy of oral edaravone.