Neuromuscular

The NeurologyLive neuromuscular disease clinical focus page offers updates and information related to the clinical care and management of individuals with neuromuscular diseases such as amyotrophic lateral sclerosis, Duchenne muscular dystrophy, cerebral palsy, and spinal muscular atrophy, as well as rare diseases. This page consists of news, podcasts, and videos about the latest FDA actions, clinical guideline updates, interviews with physicians, study and clinical trial findings, and more.

Episode 37: The Impact of Awareness Efforts in ALS

"Mind Moments," a podcast from NeurologyLive, brings you an exclusive interview with Matthew B. Harms, MD.

Case-Based Insights: Expert Perspectives on the Treatment of Adult-Onset SMA

Expert neurologists discuss patient cases involving the treatment of adult-onset spinal muscular atrophy (SMA).

NeuroVoices: Yung Chyung, MD, on the Advantages of Apitegromab in Early SMA Treatment

The chief medical officer of Scholar Rock described how the investigational apitegromab aims to fill some of the current unmet needs for patients with spinal muscular atrophy.

This Week on NeurologyLive — October 25, 2021

October 25, 2021

Article

Here's what is coming soon to NeurologyLive.

NeurologyLive Friday 5 — October 22, 2021

October 22, 2021

Article

Take 5 minutes to catch up on NeurologyLive's highlights from the week ending October 22, 2021.

Clinical Characteristic Insights in Myasthenia Gravis Reveal Treatment Insufficiencies

October 20, 2021

Article

Investigators found that women with early-onset myasthenia gravis display distinct clinical features in contrast with men with the same condition, who are more like patients with late-onset MG of both sexes.

Tofersen Falls Short in Phase 3 ALS Study, But Shows Favorable Trends

October 18, 2021

Article

Treatment of ALS with tofersen resulted in differences in total cerebrospinal fluid SOD1 protein and neurofilament light chain, both markets of target engagement and neuronal degeneration.

This Week on NeurologyLive — October 18, 2021

October 18, 2021

Article

Here's what is coming soon to NeurologyLive.

NeurologyLive Friday 5 — October 15, 2021

October 15, 2021

Article

Take 5 minutes to catch up on NeurologyLive's highlights from the week ending October 15, 2021.

This Week on NeurologyLive — October 11, 2021

October 11, 2021

Article

Here's what is coming soon to NeurologyLive.

Clinicians’ Role in Addressing the Neurologist Shortage: Jennifer Majersik, MD, MS

October 10, 2021

Video

The division chief of vascular neurology at the University of Utah discussed the individual role that clinicians and neurologists can play to increase interest in the field of neurology. [WATCH TIME: 2 minutes]

Positive Phase 1 Results, Regulatory Progress Announced for 2 Therapeutics in ALS

October 09, 2021

Article

Clinical data on the investigational therapeutics, DNL343 and SAR443820/DNL788, were presented at the 2021 Annual Northeast ALS Meeting this month.

NeurologyLive Friday 5 — October 8, 2021

October 08, 2021

Article

Take 5 minutes to catch up on NeurologyLive's highlights from the week ending October 8, 2021.