Opinion|Videos|July 3, 2024

Current and Emerging Treatment Options and Management of Duchenne Muscular Dystrophy

An expert on Duchenne muscular dystrophy reviews standard-of-care treatment options and provides clinical insights on adverse effects and safety concerns, particularly with corticosteroids.

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Video content above is prompted by the following questions:

  • Please briefly describe the current standard of care for Duchenne muscular dystrophy (DMD).
    • What are the side effects and/or safety concerns associated with long-term use of corticosteroids in patients with DMD?
    • Discuss recent approvals and ongoing studies in DMD.

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