A. Gordon Smith, MD, FAAN, discusses how to assess for treatment success and why the patient perspective is so important in deciding whether to change therapies.
FDA Approves Expanded Indication for Cerliponase Alfa to Treat CLN2 Disease in Children Under 3 Years
Episode 114: AMX0035, Phase 3 PHOENIX Study, and Amylyx's Future Drug Development
Ionis to Advance ION582 in Phase 3 Studies of Angelman Syndrome Following Positive Open-Label Data
Special Episode: FDA Approves HDAC Inhibitor Givinostat for Duchenne Muscular Dystrophy
This Week on NeurologyLive® — July 22, 2024
Amifampridine in LEMS and Beyond: Unraveling Its Therapeutic Potential