International Pompe Day 2026: Top News and Expert Insights

According to the National Organization for Rare Disorders, Pompe disease occurs in approximately 1 in 40,000 births in the United States and the Netherlands; however, in some populations, the incidence is substantially higher.¹ Over the past year, NeurologyLive® has covered news and clinical trial data updates related to the various therapies currently in development for Pompe disease and conducted interviews with experts to discern the potential for new research and treatments to affect the care paradigm.