SPOTLIGHT -
Experience with Risdiplam and Unmet Needs in SMA
James Wymer, MD discusses his firsthand experience with risdiplam and identifies a key unmet need in the treatment of spinal muscular atrophy.
Importance of Compliance and Multidisciplinary Management in SMA
An expert neurologist emphasizes the importance of medication compliance and the value of multidisciplinary management in meeting patient goals of therapy for spinal muscular atrophy.
Goals of Therapy and Treatment Selection in Adult-Onset SMA
An insight into the goals of therapy and treatment selection between oral and intrathecal medications for adult-onset spinal muscular atrophy.
Treatment Approach in SMA
A discussion of the multidisciplinary treatment approach in spinal muscular atrophy.
Diagnosis of Adult-Onset SMA
An overview of the diagnosis of spinal muscular atrophy, including prevalence, age of onset, and the role of genetic testing.
A 38-Year-Old Female with Spinal Muscular Atrophy
James Wymer, MD, provides a case overview of a 38-year-old female diagnosed with spinal muscular atrophy.
Caring for Patients With ALS: A Brief Review
Although there is no cure for ALS, there are treatments available that can improve the quality of life and prolong survival.