What to Expect at MDA’s 2025 Clinical and Scientific Conference: Barry J. Byrne, MD, PhD

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"his is the era of therapies for neuromuscular diseases. In the past year, we saw an additional few strategies that are transformative in the care of boys with DMD and we have continued to make advances in SMA care following on the enormous success of the release of Zolgensma in 2019."

This content was originally published by our sister publication, CGTLive.

The Muscular Dystrophy Association (MDA) is an organization dedicated to serving the community of patients with neuromuscular disorders, both those with muscular dystrophies and those with other types of neuromuscular disease. Each year, the organization holds the MDA Clinical & Scientific Conference to bring together physicians, clinical trial investigators, academic researchers, patient advocates, biotech executives, and other stakeholders to share and discuss the latest findings in neuromuscular disease research. This year’s meeting, which will be held from March 16 to 19, 2025, in Dallas, Texas, is notable for coinciding with the 75th anniversary of the organization itself.

Ahead of the conference, CGTLive^® had an interview with Barry J. Byrne, MD, PhD, the chief medical advisor at MDA, to learn more about what attendees can expect at this year’s event. He emphasized that the field of muscular dystrophy has recently entered the era of disease-modifying treatment after a long history of basic research, thanks in part to the FDA’s approvals of several gene therapy products for neuromuscular diseases in recent years. Furthermore, he noted that means of maximizing muscle regeneration in patients with degenerative neuromuscular diseases, real world experience with Elevidys following its 2024 expanded access approval, and tackling challenges with access to treatment or reimbursement will be among the themes at the 2025 conference.

Registration for the 2025 MDA Conference is now open! The meeting is set to be held at the Hilton Anatole, Dallas, Texas, from March 16 to 19, 2025. To register and for more information, head to www.mdaconference.org