Neuromuscular

NeurologyLive Friday 5 — September 18, 2020

September 18, 2020

Take 5 minutes to catch up on NeurologyLive's highlights from the week ending September 18, 2020.

Mary Schroth, MD: Cure SMA’s Ongoing Advocacy Initiatives

September 15, 2020

The chief medical officer at Cure SMA spoke to the ongoing work that the organization does in advocating for patients with spinal muscular atrophy, particularly for newborn screening.

NeurologyLive Friday 5 — September 11, 2020

September 11, 2020

Take 5 minutes to catch up on NeurologyLive's highlights from the week ending September 11, 2020.

Mary Schroth, MD: The Challenge of Early SMA Recognition

September 10, 2020

The chief medical officer at Cure SMA detailed the importance of having options for patients and how certain administration routes and schedules offer more personalized approaches, particularly for adult patients with SMA.

The Psychosocial Impact of COVID-19 in Neurology Departments

September 10, 2020

Leah Croll, MD, a neurology resident on the front lines of the COVID-19 pandemic, shares details from her study on the psychosocial impact on physicians and her first-hand experience.

Sabrina Paganoni, MD, PhD: CENTAUR Trial Open-Label Extension in ALS

September 09, 2020

The investigator at the Healey & AMG Center for ALS at Massachusetts General Hospital spoke to the CENTAUR open-label extension and AMX0035’s development.

Prosetin Gets Orphan Drug Status for ALS

September 09, 2020

The Project ALS-funded oral MAP4 kinase inhibitor has been described in the literature as an exceptionally potent, metabolically stable, and blood-brain barrier-penetrant compound.

Real World and Natural History Data Comparable to Placebo in DMD Trials

September 09, 2020

Researchers noted that the findings are encouraging for the use of real-world data and natural history data to augment, or possibly replace, placebo controls in DMD trials.

Leah Croll, MD: Psychosocial Implications of COVID-19 on Doctors

September 08, 2020

The neurology resident at NYU Langone described psychosocial implications that physicians faced during the COVID-19 pandemic and the toll it takes on them.

Sabrina Paganoni, MD, PhD: A Combination Approach to ALS

September 07, 2020

The investigator at the Healey & AMG Center for ALS detailed the combination of AMX0035 and other agents and how ALSFRS-R scores translate to daily life.

NeurologyLive Friday 5 — September 4, 2020

September 04, 2020

Take 5 minutes to catch up on NeurologyLive's highlights from the week ending September 4, 2020.