Neuromuscular

The NeurologyLive neuromuscular disease clinical focus page offers updates and information related to the clinical care and management of individuals with neuromuscular diseases such as amyotrophic lateral sclerosis, Duchenne muscular dystrophy, cerebral palsy, and spinal muscular atrophy, as well as rare diseases. This page consists of news, podcasts, and videos about the latest FDA actions, clinical guideline updates, interviews with physicians, study and clinical trial findings, and more.

This Week on NeurologyLive — June 14, 2021

June 14, 2021

Article

Here's what is coming soon to NeurologyLive.

NeurologyLive Friday 5 — June 11, 2021

June 11, 2021

Article

Take 5 minutes to catch up on NeurologyLive's highlights from the week ending June 11, 2021.

Advantages Advanced Practice Clinicians Can Bring to Neurology: Calli L. Cook, NP, DNP

June 11, 2021

Video

The nurse practitioner at the Woodruff School of Nursing at Emory University detailed why advanced practice clinicians should be utilized more in neurology settings.

Nusinersen Shows Improved 3-Year Survival in Infantile-Onset SMA

June 10, 2021

Article

The HINE-2 motor milestone total score in those treated with nusinersen increased steadily from a baseline mean of 1.46 to 11.86 at day 1135, representing a clinically significant change of 10.43 points.

This Week on NeurologyLive — June 7, 2021

June 07, 2021

Article

Here's what is coming soon to NeurologyLive.

Combination Therapy in ALS: Sabrina Paganoni, MD, PhD

June 06, 2021

Video

The investigator at the Healey & AMG Center for ALS at Massachusetts General Hospital discussed how adding AMX0035 to a therapeutic regimen might improve treatment of ALS.

Experts Call for Better Trial Design, Alzheimer Disease Vaccine Shows Safety, FDA Accepts IND for LION-101

June 05, 2021

Video

Neurology News Network for the week ending June 5, 2021.

NeurologyLive Friday 5 — June 4, 2021

June 04, 2021

Article

Take 5 minutes to catch up on NeurologyLive's highlights from the week ending June 4, 2021.

FDA Accepts IND for Limb-Girdle Muscular Dystrophy Gene Therapy

June 03, 2021

Article

Asklepios BioPharmaceuticals noted that it plans to initiate dosing for the LION-101 phase 1/2 clinical trial in the first half of 2022.

Phase 3 PHOENIX Study of AMX0035: Sabrina Paganoni, MD, PhD

June 01, 2021

Video

The investigator at the Healey & AMG Center for ALS at Massachusetts General Hospital discussed how the PHOENIX study expands upon the previous study, CENTAUR.