Gaining a Greater Understanding of the Global Burden of Neurologic Disorders
Published: May 21st 2024 | Updated: May 23rd 2024Bruce Leuchter, MD, a neuropsychiatrist and chief executive officer at Neurvati Neurosciences, provided insight on a recently published study showing that neurological diseases present the biggest global health threat.
ION582 Improves Cognition, Motor Function, and Communication in Phase 1/2 Trial of Angelman Syndrome
Published: May 21st 2024 | Updated: May 21st 2024ION582, delivered intrathecally into the cerebral spinal fluid with a lumbar puncture, resulted in significant improvements in cognition, fine and gross motor skills, and expressive communication.
Exploring the Association Between Brain Lesions and Takotsubo Syndrome
May 21st 2024Frederic Schaper, MD, PhD, an instructor in neurology at Brigham and Women's Hospital, discussed the complex interplay between brain lesions and takotsubo syndrome, a heart condition caused by physical and emotional triggers.
Reviewing Ravulizumab’s Long-Term Profile as New NMOSD Treatment
May 18th 2024Sean Pittock, MD, director of the Mayo Clinic Center for Multiple Sclerosis and Autoimmune Neurology detailed interim data from the open-label extension of the pivotal CHAMPION-NMOSD trial, the study that led to ravulizumab’s approval.
FDA Grants Rare Pediatric Disease Designation to DMD Gene Therapy Candidate SGT-003
May 16th 2024Solid Biosciences is expecting to provide initial safety data on SGT-003 from the first couple of pediatric patients with Duchenne muscular dystrophy enrolled in the phase 1/2 INSPIRE Duchenne trial in mid-2024.
Efficacy of Switching From to Inebilizumab in Rituximab in NMOSD: Michael Levy, MD, PhD
Published: May 16th 2024 | Updated: May 20th 2024The associate professor of neurology at Harvard Medical School talked about findings from a recent case series of patients with NMOSD initially on rituximab who then switched to inebilizumab. [WATCH TIME: 4 minutes]
The Promising Future of Gene Therapy in Treating Neurological Diseases: Michael Kaplitt, MD, PhD
May 15th 2024The professor of neurological surgery at Weill Cornell medicine talked about how gene therapy may offer a more direct and efficient pathway to develop treatments for neurological diseases like Parkinson disease. [WATCH TIME: 6 minutes]
Eisai Commences Rolling BLA for Subcutaneous Autoinjector Form of Lecanemab
May 15th 2024The subcutaneous autoinjector, which facilitates 360 mg weekly maintenance dosing of lecanemab, takes less time to administer than the approved intravenous formulation and may lead to less hospital visits and nursing care.