Opinion|Videos|July 8, 2024

Determining Treatment Success in Spinal Muscular Atrophy

Panelists share their approaches to counseling adult patients with spinal muscular atrophy (SMA) about treatment expectations.

  1. What do you consider successful therapy in an adult?

Related to this article

Collective Advocacy, Shared Priorities, and What’s Ahead at MDA 2027
Paul Melmeyer, MPP, Executive Vice President of Public Policy and Advocacy at the Muscular Dystrophy Association, discusses the Neuromuscular Advocacy Collaborative, its growing year-round presence, and what the group hopes to accomplish heading into the 2027 MDA Clinical and Scientific Conference.