Opinion|Videos|June 10, 2024

Natural History of Spinal Muscular Atrophy

Author(s)Lauren Elman, MD
Arun S. Varadhachary, MD, PhD

Panelists examine the natural history of spinal muscular atrophy (SMA), assessing the characteristic indicators of motor function deterioration and the loss of ambulatory abilities as patients advance in age.

What do we know about the natural history of SMA?
Discuss decline in motor function and loss of ambulation over time in adults.

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