Opinion|Videos|July 1, 2024

Factors Guiding Treatment Selection in Adult Spinal Muscular Atrophy

Author(s)Lauren Elman, MD
Arun S. Varadhachary, MD, PhD

Panelists explore critical considerations when choosing a treatment approach for treatment-naïve adult patients with spinal muscular atrophy (SMA), taking into account factors such as disease severity, patient preferences, and potential treatment outcomes.

What factors guide choice of therapy in treatment naïve adult patients?

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