Multidisciplinary Care and Individualized Treatment Goals in Duchenne Muscular Dystrophy

Effective management of Duchenne muscular dystrophy (DMD) relies on a multidisciplinary team approach to address the complex and evolving needs of patients. Key specialties include neurologists, cardiologists, pulmonologists, physical and occupational therapists, genetic counselors, dietitians, and social workers, all collaborating to optimize function, monitor disease progression, and support quality of life. Best practices emphasize regular communication, coordinated care plans, and early intervention to prevent complications. Treatment goals are individualized based on patient age, disease stage, functional status, and mutation type. In early ambulatory patients, goals focus on preserving mobility and delaying muscle weakness, whereas in non-ambulatory stages, priorities shift to maintaining upper limb function, respiratory support, and cardiac health. Therapy selection evolves accordingly, integrating corticosteroids, disease-modifying agents, and supportive interventions. A patient-centered, adaptable approach ensures that clinical strategies align with disease progression, maximizing both physical outcomes and overall quality of life.