Raising Awareness to Improve Early Diagnosis and Treatment of Duchenne Muscular Dystrophy: Douglas Sproule, MD, MSc
Key Details of Phase 3 ORION Study of AMX0035 in Progressive Supranuclear Palsy: Gunter Hoglinger, MD
Potential FDA Accelerated Approval for Limb-Girdle Muscular Dystrophy 2I/R9 Therapy: Douglas Sproule, MD, MSc
Balancing Safety and Efficacy in Developing Therapeutic for Rare Neuromuscular Diseases: Douglas Sproule, MD, MSc
The Evolution of RSBQ as a Standard Measure for Rett Syndrome in Clinical Trials: Walter E. Kaufmann, MD
Advancing BBP-418 in Phase 3 Settings as Potential Limb Girdle Muscular Dystrophy Treatment: Douglas Sproule, MD, MSc
CNM-Au8 Improves Survival in ALS, New Parkinson Risk Factor Identified, Pamrevlumab Falls Short in Phase 3 Study