NEUROMUSCULAR

Zolgensma, an adeno-associated virus vector-based, one-time gene therapy administered via intravenous infusion, is the first and only FDA-approved gene therapy for SMA. 
Experts shed light on the data behind the first FDA approval for spinal muscular atrophy (SMA), nusinersen, and consider what was learned through its approval.

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About NeurologyLive's Neuromuscular Clinical Focus page:

The NeurologyLive Neuromuscular Clinical Focus page provides the latest clinical updates about neuromuscular diseases, with articles and videos covering the most up-to-date advancements in the field. Visitors to the clinical focus page will find information on emerging treatment options, as well as updates from the world’s top neurology conferences and annual meetings, including key coverage on rare disorders like ALS, DMD, and MD.

Additionally, articles and video editorial from neurologists and professionals specializing in neuromuscular conditions can be found on this page, offering expert guidance on current management strategies and potential neuromuscular therapy options.