NEUROMUSCULAR

NeurologyLive's Neuromuscular Clinical Focus page focuses on the latest news and research for rare disorders like amyotrophic lateral sclerosis (ALS), Duchenne muscular dystrophy (DMD), and myasthenia gravis (MG).

FDA Approves Gene Therapy Zolgensma for Spinal Muscular Atrophy

Zolgensma, an adeno-associated virus vector-based, one-time gene therapy administered via intravenous infusion, is the first and only FDA-approved gene therapy for SMA.

Nusinersen: The First Approval for Spinal Muscular Atrophy

Experts shed light on the data behind the first FDA approval for spinal muscular atrophy (SMA), nusinersen, and consider what was learned through its approval.

The State of Charcot-Marie-Tooth Disease: An In-Depth Interview With K. Florian P. Thomas, MD

The Director of the Multiple Sclerosis and Hereditary Neuropathy Centers at Seton Hall-Hackensack Meridian School of Medicine shared insight into what clinicians should know about Charcot-Marie-Tooth disease.

Muscular Dystrophy Association Panel Calls for Expanded Newborn Screening

An MDA panel has stated that accessibility of advanced screening, the introduction of effective treatment, and the support of professional organizations could, and should, prompt the expansion of newborn screening.

Peripheral Neuropathy Associated With Fluoroquinolone Exposure is Time and Dose Dependent

Ultimately, the risk of peripheral neuropathy increased by an estimated 3% for each additional day of current fluoroquinolone exposure, maintained for up to 180 days post-exposure.

Spinal Muscular Atrophy: Palliative Concepts in Care

Impact of Bone Health on Spinal Muscular Atrophy

The Role of Nutrition in Spinal Muscular Atrophy

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About NeurologyLive's Neuromuscular Clinical Focus page:

The NeurologyLive Neuromuscular Clinical Focus page provides the latest clinical updates about neuromuscular diseases, with articles and videos covering the most up-to-date advancements in the field. Visitors to the clinical focus page will find information on emerging treatment options, as well as updates from the world’s top neurology conferences and annual meetings, including key coverage on rare disorders like ALS, DMD, and MD.

Additionally, articles and video editorial from neurologists and professionals specializing in neuromuscular conditions can be found on this page, offering expert guidance on current management strategies and potential neuromuscular therapy options.