Turning Gene Therapy Into Reality: Peter Marks, MD, PhD
March 20th 2023The director of the Center for Biologics Evaluation Research at the FDA provided an overview of the Keynote Address he gave at the 2023 Muscular Dystrophy Association Clinical and Scientific Conference. [WATCH TIME: 3 minutes]
A Balancing Challenge: Social Relationships in the Life of Adolescents With Narcolepsy
March 19th 2023Anne Marie Morse, DO, a pediatric neurologist and sleep medicine specialist at Geisinger Medical Center, talked about the challenges that adolescents with narcolepsy face in their social relationships.
FDA to Hold AdComm Meeting on Investigational DMD Treatment SRP-9001
March 18th 2023The FDA has reversed course, deciding to hold an advisory committee meeting ahead of the May 29, 2023, action date for Sarepta’s investigational DMD agent SRP-9001 (also known as delandistrogene moxeparvovec).
Inebilizumab as a Treatment for NMOSD and Autoimmune Encephalitis: Gregory Day, MD, MSc, MSCI, FAAN
March 17th 2023The neurologist at Mayo Clinic, in Jacksonville, Florida, spoke about inebilizumab as a treatment for NMOSD and other autoimmune diseases, such as encephalitis, in the ExTINGUISH trial. [WATCH TIME: 3 minutes]
The Idea Behind Using Masked 40 Hz, Light Based Brain Stimulation for Alzheimer Disease
March 16th 2023Marcus Carstensen, PhD candidate, CTO and co-founder of OptoCeutics in Copenhagen, Denmark, talked about the mechanisms of using noninvasive light technologies for Alzheimer disease treatment.
Importance of Establishing Healthy Eating Habits in Epilepsy: Orrin Devinsky, MD
March 16th 2023The director of the Comprehensive Epilepsy Center at NYU Langone discussed the importance of healthy eating habits and whether all individuals with epilepsy should consider dieting early in their life. [WATCH TIME: 4 minutes]