Neuromuscular

A novel gene therapy has demonstrated impressive early results in a small sample of 3 children with Duchenne muscular dystrophy.

A grant from the National Institute of Neurological Disorders and Stroke, which allows for concurrent phase I and II trial design review, will speed up the development of novel treatments for patients with ALS and FTD.

An expanded access program has been opened to allow patients with ALS access to BHV-0223, a sublingual formulation of riluzole, all while Biohaven Pharmaceutical prepares a new drug application for the drug.

The announcement was discouraging to many, as only 2 agents for ALS have been granted FDA approval in as many decades.

The chief medical officer and chief operating officer of Brainstorm Cell Therapeutics spoke about a host of topics related to the treatment of amyotrophic lateral sclerosis.

The treatment is the first patient-infused subcutaneous formulation of immunoglobulin to gain approval for CIDP.

Although there is no cure for ALS, there are treatments available that can improve the quality of life and prolong survival.

What neuropsychiatric conditions are relatives of people with ALS at risk for? Are other genes involved besides C9orf72?

Two more novel therapies are quickly following the first approval in 2 decades for ALS.

A genetic mutation suspected to be associated with amyotrophic lateral sclerosis risk has been confirmed through a large-scale research effort.

Serum testing for NMDAR and other autoantibodies is fraught with pitfalls, and careful clinical consideration is important.