The NeurologyLive® neuromuscular disease clinical focus page offers updates and information related to the clinical care and management of individuals with neuromuscular diseases such as amyotrophic lateral sclerosis, Duchenne muscular dystrophy, cerebral palsy, and spinal muscular atrophy, as well as rare diseases. This page consists of news, podcasts, and videos about the latest FDA actions, clinical guideline updates, interviews with physicians, study and clinical trial findings, and more.
September 1st 2025
Here's some of what is coming soon to NeurologyLive® this week.
Bone Marrow-Derived Mesenchymal Stem Cells Show Safety in ALS
October 29th 2021ALSFRS-R and FVC values were stable after cell therapy during the 3-month follow-up; however, the scores and values significantly decreased after 6 months of treatment. The data, the authors noted, warrant future assessments in ALS.
Clinical Characteristic Insights in Myasthenia Gravis Reveal Treatment Insufficiencies
October 20th 2021Investigators found that women with early-onset myasthenia gravis display distinct clinical features in contrast with men with the same condition, who are more like patients with late-onset MG of both sexes.
Clinicians’ Role in Addressing the Neurologist Shortage: Jennifer Majersik, MD, MS
October 10th 2021The division chief of vascular neurology at the University of Utah discussed the individual role that clinicians and neurologists can play to increase interest in the field of neurology. [WATCH TIME: 2 minutes]
First Patients Dosed in Trial of WVE-N531 in Duchenne Muscular Dystrophy
October 3rd 2021In preclinical mouse models lacking both dystrophin and utrophin, treatment with an agent using the company's PN chemistry resulted in 100% survival at 40 weeks, setting up the therapy for this phase 1b2/a trial.